The development of a brain tumor in a study participant led regulators to suspend a Hurler syndrome therapy in early testing ...

Universal gene‑edited CAR‑T therapies turn donor T cells into off‑the‑shelf cancer treatments, cutting delays and costs while ...

A paper published in Biology Methods and Protocols, indicates that a new computational method may help researchers identify ...

Market OverviewThe global cell and gene therapy market is undergoing rapid and transformative growth, reflecting its increasing importance in modern healthcare.The market is projected to expand at a ...

Precision DNA editing gene therapy achieves deep remissions in aggressive leukemia previously considered incurable.

After telegraphing an investigation in November, the FDA has moved to restrict the use of bluebird bio’s gene therapy Skysona in certain patients. The FDA has updated Skysona’s indication, allowing it ...

Gene therapy represents an innovative approach to treating cancer by directly modifying the genetic material within tumour cells, thereby utilising molecular mechanisms to inhibit tumour growth or ...

Orphan Drug Designation applies to approximately 50,000 Patients who predominantly suffer from severe chronic pain due ...

Biopsy specimen of a glioblastoma with prominent micovascular proliferation (formation of a mulitlayered "glomeruloid tuft", HE stain). (Jensflorian, CC BY-SA 3.0 , via Wikimedia Commons) From Philly ...

Key opportunities in the gene therapy market include treating genetic disorders and cancer, driven by rising FDA approvals and biotechnological advancements. The in vivo segment, cancer treatments, ...

A recent publication in Nature Medicine describes a novel immunotherapy targeting pancreatic cancer that has shown promising results in a first in-human phase 1/2 trial. The TACTOPS trial, which ...